My three wishes for the future of rare disease are:
1.That all the key stakeholders in the UK are able to collaborate and find the access and service solutions needed so that innovative treatments can be available to patients in a timely manner.
2.There is equity of access across the the 4 nations to the NHS and social care services needed by people with a rare disease and their families.
3.The UK is looked to as a global leader for ATMPs for patients from clinical trials to reimbursed access