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Rare Disease Innovation and Collaboration: CRDN at Health Horizons

June 27, 2019 @ 4:00 pm - 6:00 pm

Health Horizons logo Rare Disease panel by Cambridge Rare Disease Network
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Cambridge Rare Disease Network brings a Rare Disease Innovation and Collaboration panel to Cambridge Biotech Week in Partnership with Global Innovation

Cambridge Rare Disease Network (CRDN) is hosting a Rare Disease panel as part of the new Cambridge Biotech Week Health Horizons Future Healthcare Forum.

Health Horizons Future Healthcare Forum is a high calibre, two-day conference focusing on the future of the healthcare industry. Created by the Global Innovation Forum.


Over the previous 20 years, we have seen a significant change in the healthcare industry. Small molecules have been pushed out of the blockbuster limelight by biologics. Decreasing sequencing cost has allowed more targeted R&D and the use of increasingly interdisciplinary data to influence prognosis has become standard practice. All of this points to a healthcare future with an increasingly personalized approach. But how will this future come together?

Cambridge Rare Disease Network - Rare Disease Innovation and Collaboration: CRDN at Health Horizons 1


Delegates will hear from a range of experts in this field, each with a unique perspective on the future of healthcare, treatments and cures for those affected by rare diseases.

This CRDN session brings together stakeholders from research, industry, healthcare and patient groups who are at the heart of innovative breakthroughs in therapies and technology to share their expertise in co-creating healthcare today, and for the future. Hear a mix of inspirational and thought-provoking short talks and take part in a moderated discussion session.

* Prof Tim Cox – Prof of Medicine Emeritus & Director of Research, University of Cambridge  & CRDN trustee.  A clinician with a passion for solving the long and tortured business of drug discovery, development and approval for rare diseases

* Dr Tim Guilliams –  Co-founder & CEO, Healx Ltd, and Founder & trustee of CRDN. Accelerating treatments for rare diseases through AI

* Patricia Durao – Lewi – Co-founder, Cure & Action for Tay-Sachs (CATS) Foundation. Partnering in gene therapy clinical trial as a treatment for Tay- Sachs disease, Niemann-Pick Type C (NPC),  and inherited Cerebellar Ataxias

* Dr Rick Thompson – CEO, Findacure. Developing drug repurposing social impact bonds for rare diseases

Tickets purchased via CRDN for this rare disease session do not allow access to the main Health Horizons conference. For access to the Corn Exchange for the full Health Horizons experience and to access our rare disease session as part of this use 25% discount code HH25. Click here for the full agenda and here to discover more about Health Horizons.

One in 17 people will develop a rare disease at some point in their lives – that’s 3.5 million in the UK alone and 350 million globally. Most of these diseases manifest in early childhood and many are life-limiting conditions with 95% of 7000-8000 identified rare disease having no approved treatment.

The challenges are real, but not insurmountable.  We believe that innovation is key to driving development and collaboration between companies and key rare disease players, particularly expert patients,  will make that happen.

Decades of research into gene and cell therapies are now paying dividends with recent breakthroughs for conditions such as spinal muscular atrophy (SMA), thalassemia, and rare eye diseases. More than 1,000 ongoing gene and cell therapy studies are in development and we hope to see some key regulatory approvals in 2019.  Approaches employing artificial intelligence are also advancing and accelerating therapies for rare diseases with drug repurposing in the spotlight as a faster, cheaper and more efficient way to treat conditions which have largely been forgotten. This CRDN session brings together stakeholders from research, industry, healthcare and patient groups who are at the heart of these innovative breakthroughs to share their expertise in co-creating healthcare today, and for the future.


What are my transport/parking options for getting to and from the event?

The McCrum Lecture theatre is a Corpus Christi College gem; tucked away on Bene’t’ Street and just hidden behind the Eagle Pub, just a 2 minute walk from The Corn Exchange where the Health Horizons main event takes place. The nearest parking is at the Grand Arcade or Park St multi storey. Disabled badge holders can use any metered or disabled spaces on the surrounding streets. There are a few disabled spaces on Peashill opposite the tourist information office which is a minute walk away.

How can I contact the organiser with any questions?

Email jo@camraredisease.org

Do I have to bring my printed ticket to the event?

Just bring your Eventbrite ticket email or give your name on the door.

Can I update my registration information?


Is my registration fee or ticket transferrable?


Is it ok if the name on my ticket or registration doesn’t match the person who attends?

Yes. Please transfer the ticket to another name via Eventbrite if you are unable to attend


Corpus Christi College Lecture Theatre
Trumpington Street
Cambridge, England CB2 1RH United Kingdom
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