Cystic Fibrosis: From Gene to Precision Medicines 2020

In the inherited disease cystic fibrosis (CF), thick sticky mucus blocks the lungs and bowel, leading to breathing difficulties and problems digesting food. Thirty years ago, the faulty gene responsible for CF was identified. This lecture will highlight research that has led to the development of precision medicines that target the root cause of disease, which are transforming the treatment of CF.